🙌We are happy to announce we are launching our next campaign! We are now able to take the next critical step in finding a therapy for #MCOPS12 patients! In collaboration with the CHU Sainte-Justine Research Centre in Montréal, Cure MCOPS12 will establish and co-finance a Natural History Study for MCOPS12 patients.
Natural history studies collect health information from patients over time to better understand diseases and evaluate how they progress. By collecting comprehensive medical data from each individual diagnosed with MCOPS12, we can evaluate the effectiveness of potential therapeutics in clinical trials in the near future!
Once the pre-clinical development of the ASO therapy and the drug repurposing study are finished, thanks to the Natural History Study, we will have tools to measure the effectiveness of those drugs!
This Natural History Study is a KEY fundamental step for future #drugdevelopment and treatments for MCOPS12!
However, in order to finance the Natural History Study, we need to raise approximately €30,000… We ask our friends, families, and supporters for your continued support!
It’s only with the help of the greater community that we can get closer to the establishment of a treatment for MCOPS12. 💙
Please continue to SHARE with your networks about our cause and #donate as much as you can!
#rarediseases #rarediseaseawarenessmonth #rarediseaseday #gfm