We cannot express enough gratitude for the tremendous support you have shown for ALL MCOPS12 patients. Your kindness and generosity have enabled us to not only fund the proof of concept for an ASO therapy, which has the potential to give children with MCOPS12 the ability to sit unassisted or even walk someday, but also a Natural History Study. This study is a crucial first step in future drug development and treatment for ALL MCOPS12 PATIENTS!

 

As Helen Keller once said, “Alone, we can do so little; together, we can do so much.”

 

We invite you to continue supporting our non-profit organization, Cure MCOPS12, in our mission to transform the lives of ALL MCOPS12 patients and their families.

 

Our GoFundMe Page will remain open and active, as this proof of concept and natural history study are only the initial steps in developing a treatment or therapy that may one day lead to a cure for MCOPS