In just a little over a month we’ve managed to raise almost 65K!! 🙌 We are so VERY grateful to all of you who have supported us so far – Thank YOU! 💙
Our campaign for this proof of concept for the #ASO therapy will go until the end of January and we STILL NEED about 10K…
Patients with MCOPS12 and their families face various challenges and difficulties EVERY SINGLE DAY due to the symptoms caused by this disease – from having significant vision impairments to severe movement disorders (sitting, walking, turning over, crawling), and in some cases developmental delays.
If we are UNABLE to fund this treatment path, the likelihood of improving symptoms of MCOPS12 and halting further progression is significantly DECREASED. The odds of some of these children ever being able to sit unassisted or one day even being able to walk is UNLIKELY.
We believe that EVERY child with MCOPS12 should have the CHANCE to live a MORE independent life. To have the opportunity to do the things that other kids their age can do. HELP every MCOPS12 Patient like Sophia, who wants the chance to be able to improve her mobility!
Please SHARE our fundraiser with your networks and DONATE as much as you can – every little bit can make ALL THE DIFFERENCE!